Who Am I?
Who is Trang Vo?
This Phase 2 clinical trial studies boys ages 4-9 diagnosed with DMD receiving an oral, daily tablet of EDG-5506.
What is Edgewise Lynx?
Commonly seen in males, this disease affects the muscles, leading to muscle wasting and a worsening with time.
Duchenne muscular dystrophy (DMD)
Woah - I'm high up here! This destination in downtown Atlanta can "turn" you into a big fan of the city.
What is SkyView Atlanta?
The principles of this training help assure safety, integrity, and quality of clinical trials. You can find this in CITI.
What is Good Clinical Practice (GCP)?
I can speak Mandarin and lived in China for a while. I'll usually greet you by saying your name with joy and enthusiasm. Did you also know I'm a CPhT?
Who is Christian Hanson?
HOPEfully you like fish! This IV infusion study measures the safety and tolerability of the name of this IP administered every 3 months in males ages 10 and older.
What is CAP-1002 (Capricor HOPE-3)?
What is Spinal muscular atrophy (SMA)?
This small stretch of I-75/85 bends you around one of the nation's best trauma centers. It may be one of the worst traffic areas in the city.
What is the Grady Curve?
If you want to know who is allowed to complete a procedure in a study, this document in the ISF will help you find this out.
What is a Delegation of Authority (DOA) log?
I am an RDR original staff member, the longest employed in my role. You need me to help your patients show off their muscle and lung strength. I gave a talk about Spirometry recently.
Who is Lynette Slovensky?
In 2023, this study's drug reached statistical significance. The participants were unblinded to their group assignment and are either going to receive the drug as EAP or OLE at RDR.
What is AT (Applied Therapeutics)?
Features of this disorder include developmental delays, intellectual disabilities, balance, and speech impairments. You'll generally see the patient smiling. Loss of function is typically due to the loss of function of a gene called UBE3A.
What is Angelman syndrome?
The A is for grade! Although you may not recall its first name was Dwarf House, this popular restaurant changed its menu from burgers to poultry items in 1967.
What is Chick-fil-A?
Dr. James Lind is celebrated on this day as the first person to run a controlled trial in 1774. He evaluated various diets in sailors with scurvy.
What is Clinical Trials Day (May 20th)?
I grew up around Philadelphia and bounced around different places until I landed at Emory and now RDR. Hopefully you are not allergic to me!
Who is Dr. Samata Kamireddy?
Let's deliver some good results! This MAD study consists of IV infusions of IP to treat DMD amenable to Exon 51 skipping and evaluate dystrophin protein levels in muscle tissue.
What is the Dyne251-DMD-201 (DELIVER) study?
This first of two types of this disease consists (in its classic form) of muscle weakness and wasting, including prolonged muscle tensing. Beside the muscles, it can also affect the hearts, eyes, CNS, and endocrine system.
What is Myotonic dystrophy type 1 (DM1)?
Welcome to Broadway! This lavish performing arts venue hosts events such as the ballet, musicals, and concerts in Midtown.
What is the Fox Theatre?
In certain clinical trials, the sponsor is focusing on safety and efficacy of the IP targeting a decent number of patients for a relatively short amount of time. Generally only 33% of studies make it out of this phase.
What is Phase 2?
I recently moved from California to Atlanta. I have spent many years working in research. Later this year I will be going back to visit to see Beyonce in concert.
Who is Tiffany Bennett?
This isn't geometry! This study skips the IP and tells the PI to assess devices. By looking at both healthy and diagnosed patients, we can get results that are "very HOT"!
What is the Vertex Myotonic Dystrophy (VX22-MDO-801) study?
This inherited condition causes progressive weakness and wasting of skeletal and cardiac muscles. This is similar to DMD but this progresses later and at a slower rate.
What is Becker muscular dystrophy (BMD)?
As a result of a fire during the Civil War in 1864, the city gained this animal symbol.
What is a phoenix?
This document published in 1978 identifies three basic principles for human subjects research, including respect for persons, beneficence, and justice.