Type of Technology
What kind of diseases is it used for?
Cystic fibrosis, Sickle cell, hemophilia
What is a GMO?
Genetically modified organism
What is the main goal of gene therapy?
To replace unhealthy genes with functional ones.
Why might one be against gene therapy?
Risks and inconsistent results
What does vectors like viruses deliver?
Healthy genes
What is the main benefit of gene therapy?
Cure diseases at their root.
What does gene therapy do?
Replace, Repair, or Add genes in cells
What was one successful example of gene therapy?
Luxturna
What is one way of delivering new genes to a person ?
Viral Vectors
What was one of the risks we went over?
Tissue/organ damage, Risk of infection, Cancer, an adverse response or organ failure.